Tag: Cystic Fibrosis

Innovation, Patient Experience

A Move to Cut Drug Prices Has Patients With Rare Diseases Worried

August 30, 2023

Via: Kaiser Health News

For people with cystic fibrosis, like Sabrina Walker, Trikafta has been a life-changer. Before she started taking the drug, she would wind up in the hospital for weeks at a time until antibiotics could eliminate the infections in her lungs. […]

Innovation, Research

Small package, big potential to help cell-based therapies

June 6, 2022

Via: ScienceDaily

Cell-based therapies have long been thought of as an alternative treatment option for patients with a range of diseases caused by organ and tissue failure, inclusive of heart attack, diabetes, corneal blindness, and cystic fibrosis. While great in theory, in […]

Innovation, Research

New antibiotic fights drug-resistant bacteria without notable toxic side-effects

May 4, 2020

Via: The Medical News

Through serendipity, researchers at the University of Pittsburgh Graduate School of Public Health considerably reduced the toxicity of a potential antibiotic against the most feared drug-resistant bacteria, while also improving its stability in fighting infections. The new antibiotic -; administered […]

Innovation, Research

Researchers investigate recessive genetic disorder that leads to childhood blindness

July 23, 2018

Via: The Medical News

Our genome is made up of 20,000 genes, all of which may cause disease. At present, 4,141 genes have been identified as being responsible for genetic abnormalities, leaving around 16,000 genes with unknown implication in disease. Researchers from the University […]


How Can We Encourage More Organ Donations?

September 28, 2017

Via: Forbes

Now that the malevolent Graham-Cassidy bill has died, my focus is returning to helping people in more positive ways. One is to come together and help each other through organ donation. The wait list for organs has been growing much […]

Innovation, Regulatory

FDA Approves New Cystic Fibrosis Drug

July 3, 2015

Via: time health

(WASHINGTON)—Federal health officials have approved a new combination drug for the most common form of cystic fibrosis, the debilitating inherited disease that causes internal mucus buildup, lung infections and early death. But it will come at a steep price — […]